The first clinical application of gene therapy over a 4 year old girl was for_________?

Correct answer: A. Adenosine deaminase deficiency

  • A. Adenosine deaminase deficiency
  • B. Adenosine deficiency
  • C. Growth deficiency
  • D. Adenine deficiency

Explanation

The first widely recognised clinical gene-therapy trial treated severe combined immunodeficiency caused by adenosine deaminase deficiency by introducing a functional ADA gene into the patient's cells. Adenosine deficiency is the likely distractor because it sounds similar, but the disorder specifically involves the ADA enzyme.

Last updated

Related questions